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書誌情報 | ファイル |
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Minimizing off-Target Mutagenesis Risks Caused by Programmable Nucleases. Ishida, Kentaro; Gee, Peter; Hotta, Akitsu (2015-10-16) International journal of molecular sciences, 16(10): 24751-24771 | |
Site-specific randomization of the endogenous genome by a regulatable CRISPR-Cas9 piggyBac system in human cells Ishida, Kentaro; Xu, Huaigeng; Sasakawa, Noriko; Lung, Mandy Siu Yu; Kudryashev, Julia Alexandra; Gee, Peter; Hotta, Akitsu (2018-01-10) Scientific Reports, 8 | |
Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9 Li, Hongmei Lisa; Fujimoto, Naoko; Sasakawa, Noriko; Shirai, Saya; Ohkame, Tokiko; Sakuma, Tetsushi; Tanaka, Michihiro; Amano, Naoki; Watanabe, Akira; Sakurai, Hidetoshi; Yamamoto, Takashi; Yamanaka, Shinya; Hotta, Akitsu (2015-01-13) Stem Cell Reports, 4(1): 143-154 | |
Efficient ssODN-Mediated Targeting by Avoiding Cellular Inhibitory RNAs through Precomplexed CRISPR-Cas9/sgRNA Ribonucleoprotein Kagita, Akihiro; Lung, Mandy S.Y.; Xu, Huaigeng; Kita, Yuto; Sasakawa, Noriko; Iguchi, Takahiro; Ono, Miyuki; Wang, Xiou H.; Gee, Peter; Hotta, Akitsu (2021-03-11) Stem Cell Reports | |
A Patient-derived iPSC Model Revealed Oxidative Stress Increases Facioscapulohumeral Muscular Dystrophy-causative DUX4 Sasaki-Honda, Mitsuru; Jonouchi, Tatsuya; Arai, Meni; Hotta, Akitsu; Mitsuhashi, Satomi; Nishino, Ichizo; Matsuda, Ryoichi; Sakurai, Hidetoshi (2018-12-01) Human Molecular Genetics, 27(23): 4024-4035 | |
Srf destabilizes cellular identity by suppressing cell-type-specific gene expression programs Ikeda, Takashi; Hikichi, Takafusa; Miura, Hisashi; Shibata, Hirofumi; Mitsunaga, Kanae; Yamada, Yosuke; Woltjen, Knut; Miyamoto, Kei; Hiratani, Ichiro; Yamada, Yasuhiro; Hotta, Akitsu; Yamamoto, Takuya; Okita, Keisuke; Masui, Shinji (2018-04-11) Nature Communications, 9 | |
Focal Transplantation of Human iPSC-Derived Glial-Rich Neural Progenitors Improves Lifespan of ALS Mice Kondo, Takayuki; Funayama, Misato; Tsukita, Kayoko; Hotta, Akitsu; Yasuda, Akimasa; Nori, Satoshi; Kaneko, Shinjiro; Nakamura, Masaya; Takahashi, Ryosuke; Okano, Hideyuki; Yamanaka, Shinya; Inoue, Haruhisa (2014-06) Stem Cell Reports, 3(2): 242-249 | |
Calcium dysregulation contributes to neurodegeneration in FTLD patient iPSC-derived neurons. Imamura, Keiko; Sahara, Naruhiko; Kanaan, Nicholas M.; Tsukita, Kayoko; Kondo, Takayuki; Kutoku, Yumiko; Ohsawa, Yutaka; Sunada, Yoshihide; Kawakami, Koichi; Hotta, Akitsu; Yawata, Satoshi; Watanabe, Dai; Hasegawa, Masato; Trojanowski, John Q.; Lee, Virginia M.-Y.; Suhara, Tetsuya; Higuchi, Makoto; Inoue, Haruhisa (2016-10-10) Scientific Reports, 6 | |
Generation of a transgene-free iPSC line and genetically modified line from a facioscapulohumeral muscular dystrophy type 2 (FSHD2) patient with SMCHD1 p.Lys607Ter mutation Sasaki-Honda, Mitsuru; Kagita, Akihiro; Jonouchi, Tatsuya; Araki, Toshiyuki; Hotta, Akitsu; Sakurai, Hidetoshi (2020-08) Stem Cell Research, 47 | |
Characterization of hiPSC-Derived Muscle Progenitors Reveals Distinctive Markers for Myogenic Cell Purification Toward Cell Therapy Nalbandian, Minas; Zhao, Mingming; Sasaki-Honda, Mitsuru; Jonouchi, Tatsuya; Lucena-Cacace, Antonio; Mizusawa, Takuma; Yasuda, Masahiko; Yoshida, Yoshinori; Hotta, Akitsu; Sakurai, Hidetoshi (2021-04) Stem Cell Reports, 16 |