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Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9 Li, Hongmei Lisa; Fujimoto, Naoko; Sasakawa, Noriko; Shirai, Saya; Ohkame, Tokiko; Sakuma, Tetsushi; Tanaka, Michihiro; Amano, Naoki; Watanabe, Akira; Sakurai, Hidetoshi; Yamamoto, Takashi; Yamanaka, Shinya; Hotta, Akitsu (2015-01-13) Stem Cell Reports, 4(1): 143-154 | |
Early pathogenesis of Duchenne muscular dystrophy modelled in patient-derived human induced pluripotent stem cells. Shoji, Emi; Sakurai, Hidetoshi; Nishino, Tokiko; Nakahata, Tatsutoshi; Heike, Toshio; Awaya, Tomonari; Fujii, Nobuharu; Manabe, Yasuko; Matsuo, Masafumi; Sehara-Fujisawa, Atsuko (2015-08-20) Scientific reports, 5 | |
Induction of functional xeno-free MSCs from human iPSCs via a neural crest cell lineage Kamiya, Daisuke; Takenaka-Ninagawa, Nana; Motoike, Souta; Kajiya, Mikihito; Akaboshi, Teppei; Zhao, Chengzhu; Shibata, Mitsuaki; Senda, Sho; Toyooka, Yayoi; Sakurai, Hidetoshi; Kurihara, Hidemi; Ikeya, Makoto (2022) npj Regenerative Medicine, 7 | |
A Patient-derived iPSC Model Revealed Oxidative Stress Increases Facioscapulohumeral Muscular Dystrophy-causative DUX4 Sasaki-Honda, Mitsuru; Jonouchi, Tatsuya; Arai, Meni; Hotta, Akitsu; Mitsuhashi, Satomi; Nishino, Ichizo; Matsuda, Ryoichi; Sakurai, Hidetoshi (2018-12-01) Human Molecular Genetics, 27(23): 4024-4035 | |
Generation of a transgene-free iPSC line and genetically modified line from a facioscapulohumeral muscular dystrophy type 2 (FSHD2) patient with SMCHD1 p.Lys607Ter mutation Sasaki-Honda, Mitsuru; Kagita, Akihiro; Jonouchi, Tatsuya; Araki, Toshiyuki; Hotta, Akitsu; Sakurai, Hidetoshi (2020-08) Stem Cell Research, 47 | |
Characterization of hiPSC-Derived Muscle Progenitors Reveals Distinctive Markers for Myogenic Cell Purification Toward Cell Therapy Nalbandian, Minas; Zhao, Mingming; Sasaki-Honda, Mitsuru; Jonouchi, Tatsuya; Lucena-Cacace, Antonio; Mizusawa, Takuma; Yasuda, Masahiko; Yoshida, Yoshinori; Hotta, Akitsu; Sakurai, Hidetoshi (2021-04) Stem Cell Reports, 16 | |
Recapitulation of Extracellular LAMININ Environment Maintains Stemness of Satellite Cells In Vitro Ishii, Kana; Sakurai, Hidetoshi; Suzuki, Nobuharu; Mabuchi, Yo; Sekiya, Ichiro; Sekiguchi, Kiyotoshi; Akazawa, Chihiro (2018-02-13) Stem Cell Reports, 10(2): 568-582 | |
A muscle fatigue-like contractile decline was recapitulated using skeletal myotubes from Duchenne muscular dystrophy patient-derived iPSCs Uchimura, Tomoya; Asano, Toshifumi; Nakata, Takao; Hotta, Akitsu; Sakurai, Hidetoshi (2021-06) Cell Reports Medicine, 2(6) | |
In vitro modeling of paraxial mesodermal progenitors derived from induced pluripotent stem cells. Sakurai, Hidetoshi; Sakaguchi, Yasuko; Shoji, Emi; Nishino, Tokiko; Maki, Izumi; Sakai, Hiroshi; Hanaoka, Kazunori; Kakizuka, Akira; Sehara-Fujisawa, Atsuko (2012-10-24) PloS one, 7(10) | |
Orai1–STIM1 Regulates Increased Ca²⁺ Mobilization, Leading to Contractile Duchenne Muscular Dystrophy Phenotypes in Patient-Derived Induced Pluripotent Stem Cells Uchimura, Tomoya; Sakurai, Hidetoshi (2021) Biomedicines, 9(11) |
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